Wednesday, August 17, 2022

APOLLO Hits A Bullseye, And Alnylam Logs Another Major Clinical Win

Alnylam Pharmaceuticals (NASDAQ:ALNY) has already built an enviable record of clinical trial wins, and the company added another to the record books on August 3, with the news of success in the APOLLO-B study of patisiran (marketed as Onpattro).

The APOLLO-B study wasn't a make-or-break trial for Alnylam, but it was nevertheless a highly significant, high-risk/high-reward study for this leader in RNAi biotechnology. This successful outcome, assuming eventual FDA approval in 2023, brings substantially more addressable revenue into play with a market (hereditary ATTR amyloidosis characterized by cardiomyopathy, or hATTR-CM) that is at least 2x and quite possibly 3x or larger than the current hATTR polyneuropathy market that Onpattro serves.

I was already relatively bullish on Alnylam going into this trial read-out, so the impact to my fair value is perhaps less dramatic than for other analysts, but with a fair value of around $230 and multiple clinical read-outs over the next two years that could unlock more value, I believe these are still shares worth owning for investors willing and able to take the elevated risk that goes with biotech investing.

 

Read the full article here: 

APOLLO Hits A Bullseye, And Alnylam Logs Another Major Clinical Win

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